Hereditary amyloidosis (hATTR)

Talking to your family members about your hATTR amyloidosis diagnosis is an important first step in your disease journey. You can help your family members…

The FDA announced that it has approved patisiran infusion for the treatment of patients with peripheral nerve disease caused by hereditary transthyretin-mediated…

Steven R. Zeldenrust, age 56, of Rochester, passed away on Wednesday, July 10, 2019, after a long battle with cancer. Steve is survived by his wife of 31 years, Deb…

In an interview with Rare Disease Report, Mathew Maurer, MD, Arnold and Arlene Professor of Cardiology at Columbia University, explained the standard of care and…

Hereditary transthyretin(TTR)-related amyloidosis (ATTRm amyloidosis) is an endemic/non-endemic, autosomal-dominant, early- and late-onset, rare, progressive…

Transthyretin amyloidosis is a slowly progressive condition characterized by the buildup of abnormal deposits of a protein called amyloid (amyloidosis) in the body'…