ATTR amyloidosis drug pipeline: silencers & stabilizers

Source
Patsnap

Transthyretin amyloidosis is driving intensive pharmaceutical IP activity across four mechanistically distinct modalities — RNAi silencing, small-molecule stabilization, antibody immunotherapy, and CRISPR gene editing. This analysis maps the patent landscape, identifies the dominant assignees, and highlights combination strategies emerging as the next frontier in ATTR treatment.