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Key TakeawaysATTR-CM is a rare heart failure type caused by transthyretin protein buildup, leading to heart muscle thickening and symptoms such as shortness of…

Accurate differentiation between light-chain (AL) amyloidosis and transthyretin-mediated amyloid cardiomyopathy (ATTR-CM) is critical for effective patient…

The objective of this study is to determine the association of clinically prescribed, on-label, TTR stabilizing therapy (e.g. tafamidis or acoramidis) with levels…

Long trips can be stressful, especially when you’re living with a rare disease like amyloidosis. Symptoms vary from person to person, and the disease can affect…

Key TakeawaysAmyloidosis can cause balance problems in several ways, including nerve damage, low blood pressure, and fatigue, which can make everyday activities…

Key TakeawaysTransthyretin amyloid cardiomyopathy (ATTR-CM) is a type of heart disease caused by abnormal protein buildup in the heart, but its symptoms often look…

Rare diseases tend to remain under-discussed, underfunded, and underdiagnosed. One such condition is Amyloidosis, a collection of rare and potentially fatal…

– NXC-201 demonstrated a complete response (CR) rate of 75% (15/20) (at s/u IFE(-) level) by independent review committee –– In four out of five pending patients,…

AbstractTransthyretin amyloidosis (ATTR) with heart involvement is a progressive, life-threatening condition characterized by amyloid fibril deposition in the…

Carbon-11 Pittsburgh compound B (C-11 PiB) PET/CT demonstrates robust capability for detecting cardiac amyloidosis and accurately differentiating its subtypes,…