Diflunisal Is Effective in Hereditary ATTR, Study Confirms

Source
Rare Disease Advisor

The efficacy of diflunisal for the treatment of hereditary transthyretin amyloidosis (ATTR) was confirmed by data from the Swedish ATTR registry, according to a recent study published in Amyloid.

These real-world findings align with a pivotal clinical trial (NCT00294671) completed in 2012 that tested the effect of the treatment on familial amyloidosis.

The study’s authors said that these results offer “long-term real-world evidence” confirming the efficacy of diflunisal.