CS Blogs
Sep 30, 2024
QUINCY, Mass., Sept. 30, 2024 /PRNewswire/ -- Today, the National Organization for Rare Disorders (NORD®) announced two new requests for proposal (RFP) for…
Sep 30, 2024
Alnylam Pharmaceuticals, Inc. News− Echocardiographic and Cardiac Biomarker Data From the HELIOS-B Study Presented Today Support the Potential of Vutrisiran in…
Sep 30, 2024
People with hereditary transthyretin amyloidosis (hATTR), a group of diseases that includes familial amyloid polyneuropathy (FAP), have significantly shorter nerve…
Sep 29, 2024
In collaboration with F Hoffmann-la Roche & Co Ltd we have developed a new chemical entity, carboxy pyrrolidone hexanoyl pyrrolidone carboxylic acid (CPHPC),…
Sep 24, 2024
Key takeaways:ALXN2220, a novel investigational depleter monoclonal antibody, was granted fast track designation by the FDA.It is designed for the treatment of…
Sep 20, 2024
BackgroundImmunoglobulin light-chain amyloidosis is a relatively rare condition with a worldwide incidence of 5.1–12.8 cases per million person-years (Baker, 2022…
Sep 19, 2024
A 71-year-old healthy White male presented in 2010 with intermittent redness in the right eye nasally for 10 years. On examination, corrected visual acuity was 20/…
