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Webinar Session: Wednesday, February 25th at 6 PM (ET) Zoom Meeting(These sessions will not be recorded due to patient involvement and HIPAA laws)To Register …

License agreement leverages UCB’s expertise in antibody drug discovery to support Refold Therapeutics' ambition of providing better treatments for patients…

Join NORD’s New York Rare Action Network (RAN) for an advocacy event in Albany at the State Capitol on Tuesday, February 24 from 9:30am to 4pm. This is your chance…

Nationwide initiative encourages health-care providers to boost rare-disease knowledge and early diagnosis  BOSTON and NORWELL, Mass., FEB 23, 2026…

Follow Katherine through a yoga lesson aimed to increase strength, flexibility, and balance without straining. Movements are gentle to accommodate various physical…

An easily accessible diagnostic test called pain-related evoked potentials with concentric electrodes (PrEP-CE) may help detect the onset of hereditary…

The Food and Drug Administration (FDA) will host Rare Disease Day, a virtual public meeting, on Monday, February 23, 2026 in global observance of Rare Disease Week…

Professor Cappelli, what were the reasons behind this conference?The initiative was born from the need to address a fundamental issue: with the arrival of highly…

Transthyretin amyloid cardiomyopathy (ATTR-CM) has been traditionally considered a rare and inexorably fatal condition. However, the development of therapies able…

TULSA, Okla. -Cardiac amyloidosis, once widely considered a fatal diagnosis, is now being detected earlier and treated with newly approved medications that doctors…