News

Aerska, a startup developing treatments to silence the problematic genes that cause various brain diseases, has raised $39 million in financing, it told STAT…

ransthyretin (TTR) amyloid cardiomyopathy (ATTR-CM) is a progressive, often fatal disease. TTR stabilizers bind directly to TTR, inhibiting tetramer dissociation…

bstractATTR amyloidosis patient with initial atrial capture failure showed delayed threshold improvement over time. Stable current of injury and impedance guided…

BackgroundElvis, Joe’s son in law, has been diagnosed with a rare and serious kidney disease called MGRS (Monoclonal Gammopathy of Renal Significance) —…

Harvard Medical School’s (HMS) UDN and Countway Library of Medicine are very excited to invite you to our 2026 February Rare Disease Month Programming. For the most…

A rare and potentially fatal form of heart disease known as transthyretin amyloid cardiomyopathy, or ATTR-CM, is increasingly drawing clinical attention as…

Amyloidosis occurs when abnormal, misfolded proteins deposit in different parts of the body, including the carpal tunnel in the wrist. It often builds up in the…

NEW YORK—In 2002, Don Brockman was diagnosed with amyloidosis. The following year, he and his wife launched the nonprofit Amyloidosis Foundation, and in 2007,…

The success rate of left atrial appendage closure to prevent stroke was high and the rate of complications was low in patients with cardiac amyloidosis, according…

This article is a preprint and has not been peer-reviewed [what does this mean?]. It reports new medical research that has yet to be evaluated and so should not be…