Jan 23, 2025
As populations age, the need for informal caregivers is increasing. As individuals step up to provide care for loved ones in need, they face their own mental health…
Jan 22, 2025
ARC Executive Director of Research Kristen Hsu presented the most current updates for the clinical trial landscape, with a focus on ATTR amyloidosis. Kristen will…
Sep 30, 2024
QUINCY, Mass., Sept. 30, 2024 /PRNewswire/ -- Today, the National Organization for Rare Disorders (NORD®) announced two new requests for proposal (RFP) for…
Sep 30, 2024
Alnylam Pharmaceuticals, Inc. News− Echocardiographic and Cardiac Biomarker Data From the HELIOS-B Study Presented Today Support the Potential of Vutrisiran in…
Sep 30, 2024
People with hereditary transthyretin amyloidosis (hATTR), a group of diseases that includes familial amyloid polyneuropathy (FAP), have significantly shorter nerve…
Sep 30, 2024
The National Organization for Rare Disorders (NORD) announced two new requests for proposal (RFP) for grant funding related to Amyloidosis and Levy-Yeboa Syndrome (…
Sep 29, 2024
In collaboration with F Hoffmann-la Roche & Co Ltd we have developed a new chemical entity, carboxy pyrrolidone hexanoyl pyrrolidone carboxylic acid (CPHPC),…
Sep 26, 2024
Since starting HeartValveSurgery.com nearly twenty years ago, I have learned a lot about the heart. However, it was not until I received this email from David…
Sep 24, 2024
Key takeaways:ALXN2220, a novel investigational depleter monoclonal antibody, was granted fast track designation by the FDA.It is designed for the treatment of…
Sep 20, 2024
BackgroundImmunoglobulin light-chain amyloidosis is a relatively rare condition with a worldwide incidence of 5.1–12.8 cases per million person-years (Baker, 2022…