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The Food and Drug Administration (FDA) will host Rare Disease Day, a virtual public meeting, on Monday, February 23, 2026 in global observance of Rare Disease Week…

Professor Cappelli, what were the reasons behind this conference?The initiative was born from the need to address a fundamental issue: with the arrival of highly…

Transthyretin amyloid cardiomyopathy (ATTR-CM) has been traditionally considered a rare and inexorably fatal condition. However, the development of therapies able…

TULSA, Okla. -Cardiac amyloidosis, once widely considered a fatal diagnosis, is now being detected earlier and treated with newly approved medications that doctors…

On 21 February, Lachlan Guyot and Henry Mayjor will be taking on the iconic Rottnest Channel Swim, swimming from Cottesloe to Rottnest Island as a duo team.This…

Driven by accelerating diagnosis of ATTR cardiomyopathy, sustained reliance on cost-effective chemotherapy, and rapid uptake of disease-modifying therapies in North…

Hear from a current student in the Clinical & Translational Research Certificate Program as they reflect on their experience in the program and the impact it…

The Transthyretin Amyloidosis – Quality of Life Questionnaire (ATTR-QOL) can effectively capture the multidimensional effect of ATTR, according to a new study…

Amyloid plaques accumulate years before dementia, driven by release of the Aβ peptide from amyloid precursor protein (APP) in neurons. Now, new evidence points to…

ORLANDO, Fla. - Cardiac amyloidosis is a systemic disorder that affects the heart and can also affect other organs such as the kidneys and nervous system.…