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AbstractBackground and Objectives: Hereditary transthyretin amyloidosis (ATTRv) is a rare disease caused by pathogenic variants in the transthyretin (TTR) gene.…

Insulin-derived amyloidosis is a rare form of localised amyloidosis resulting from the aggregation of exogenous insulin into subcutaneous amyloid fibrils at…

AbstractAntibodies directed at the amyloid-β peptide offer the prospect of disease-modifying therapy for early-stage Alzheimer disease but also carry the risk of…

We are raising funds in loving memory of our mum, who sadly passed away from cardiac amyloidosis on 10/12/2025.Amyloidosis is a rare and often misunderstood…

Amyloidosis is a rare, chronic condition in which abnormal proteins bunch together to form amyloid deposits. These deposits can build in certain body organs such as…

Carlisle, PA…  Now in its third decade of doing good for those impacted by Amyloidosis, the Chip Miller Amyloidosis Foundation (CMAF) works year-round to raise…

NORD and Yale Genetics are hosting a Rare Disease Day celebration at the Yale Peabody Museum! Join us for a night of community building & connection. Attendees…

Join NORD’s Pennsylvania Rare Action Network for a virtual Rare Disease Day celebration on Friday, February 20 from 12pm to 1:10pm ET

Net cash used in operating and investing activities was $23.3 million and $163.7 million for the fourth quarter and full year of 2025, respectively; quarter-end…

Isatuximab monotherapy resulted in promising hematologic response rates with a good safety profile among patients with relapsed/refractory (R/R) light chain (AL)…